Rare Diseases

• From the National Institutes of Health
• MEDLINE Search (National Library of Medicine) - Access to over 15 million citations to biomedical articles
• Rare Diseases Terms (Office of Rare Diseases)

• Treatment
• Gene Therapy for Cancer: Questions and Answers (National Cancer Institute)
• OOPD Frequently Asked Questions (Food and Drug Administration)
• Orphan Products: Hope for People with Rare Diseases (Food and Drug Administration)

• Research
• About the Human Genome Project (National Human Genome Research Institute)

• Dictionaries/Glossaries
• Terms and Definitions (Office of Rare Diseases)

• Directories
• Genetic and Rare Diseases Information Center (Office of Rare Diseases)
• Other Sources of Rare Disease/Orphan Product Information (Food and Drug Administration)

• Organizations
• Food and Drug Administration, Office of Orphan Products Development
• Office of Rare Diseases

• Law and Policy
• FDA Fights Rare Diseases: New Help for Patients without Treatments (Food and Drug Administration)
  Also available in: Spanish