ClinicalTrials.gov
skipnavHome|Search|Browse|Resources|Help|What's New|About

Browse : By Condition : By Disease Heading : Rare Diseases : Lysosomal Storage Diseases, Nervous System


Include trials that are no longer recruiting patients.

13 studies were found.
1.RecruitingReplagal Enzyme Replacement Therapy for Children with Fabry Disease
Condition: Fabry Disease
2.RecruitingAlternative Dosing and Regimen of Replagal to Treat Fabry Disease
Condition: Fabry Disease
3.RecruitingExpanded access use of Myozyme (alglucosidase alfa) in patients with infantile-onset Pompe disease
Conditions: Glycogen Storage Disease Type II; Glycogenosis 2
4.RecruitingAn Open-Label Clinical Trial of Replagal Enzyme Therapy in Children Ages 7-17 Years with Fabry Disease
Condition: Fabry Disease
5.RecruitingRegistry of Fabry Disease - A Multicenter Observational Study
Condition: Fabry Disease
6.RecruitingOGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients with Neuronopathic Gaucher Disease
Condition: Gaucher Disease
7.RecruitingNervous System Degeneration in Glycosphingolipid Storage Disorders
Conditions: Gangliosidoses; Gaucher Disease
8.RecruitingThe Natural History and Pathogenesis of Mucolipidosis Type IV
Condition: Mucolipidosis Type IV
9.RecruitingPhase II Randomized Study of Alendronate Sodium for Osteopenia in Patients with Gaucher's Disease
Conditions: Gaucher's Disease; Osteopenia
10.RecruitingPhase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Condition: Gaucher's Disease
11.RecruitingAnalysis of the Nervous System in Patients with Fabry's Disease
Condition: Fabry's Disease
12.RecruitingEffects of Enzyme Replacement in Gaucher's Disease
Condition: Gaucher's Disease
13.RecruitingGenetic Studies of Lysosomal Storage Disorders
Conditions: Gaucher's Disease; Lysosomal Storage Disease

line
U.S. National Library of Medicine, Contact NLM Customer Service
National Institutes of Health, Department of Health & Human Services
Copyright, Privacy, Accessibility, Freedom of Information Act